Geberhiwot, T., Wasserstein, M., Wanninayake, S., Bolton, S. C., Dardis, A., Lehman, A., Lidove, O., Dawson, C., Giugliani, R., Imrie, J., Hopkin, J., Green, J., de Vicente Corbeira, D., Madathil, S., Mengel, E., Ezgü, F., Pettazzoni, M.,
Sjouke, B.,
Hollak, C., Vanier, M. T.,
& 2 othersMcGovern, M. & Schuchman, E.,
Dec 2023,
In: Orphanet journal of rare diseases. 18,
1,
p. 85 85.
Research output: Contribution to journal › Article › Academic › peer-review