Original languageEnglish
Article number383
JournalOrphanet journal of rare diseases
Volume17
Issue number1
DOIs
Publication statusPublished - 1 Dec 2022

    Research areas

  • Fabry disease, Focus group discussions, Gaucher disease type 1, Gene therapy, Lysosomal storage diseases, Mucopolysaccharidosis type III, Qualitative research

ID: 27498912