Research interests

Regulatory science, rare diseases, orphan drugs

Research output

  1. Modified Delphi procedure-based expert consensus on endpoints for an international disease registry for Metachromatic Leukodystrophy: The European Metachromatic Leukodystrophy initiative (MLDi)

    Research output: Contribution to journal › Article › Academic › peer-review

  2. Effectiveness and safety of mexiletine in patients at risk for (recurrent) ventricular arrhythmias: a systematic review

    Research output: Contribution to journal › Article › Academic › peer-review

  3. Author Reply

    Research output: Contribution to journal › Comment/Letter to the editor › Academic

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