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Research output

1. Disease burden and management of Crigler-Najjar syndrome: Report of a world registry

   Research output: Contribution to journal › Article › Academic › peer-review

2. What’s next in gene therapy for Crigler-Najjar syndrome?

   Research output: Contribution to journal › Editorial › Academic › peer-review

3. Efficacy of AAV8-hUGT1A1 with Rapamycin in neonatal, suckling, and juvenile rats to model treatment in pediatric CNs patients

   Research output: Contribution to journal › Article › Academic › peer-review

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